Farmaci orfani e malattie rare: la situazione in Italia. Farmeconomia. Health economics and therapeutic pathways, [S. l.], v. 2, n. 4, p. 261–266, 2001. DOI: 10.7175/fe.v2i4.738. Disponível em: https://journals.seedstm.com/index.php/FE/article/view/738. Acesso em: 29 oct. 2025.