Farmaci orfani e malattie rare: un confronto internazionale delle normative di riferimento. Farmeconomia. Health Economics and Therapeutic Pathways, [S. l.], v. 2, n. 3, p. 185–193, 2001. DOI: 10.7175/fe.v2i3.732. Disponível em: https://journals.seedstm.com/index.php/FE/article/view/732. Acesso em: 29 dec. 2025.